NHS drugs go-ahead offers lifeline to children with rare muscle-wasting disease

Medicines watchdog approves two treatments for patients with spinal muscular atrophy Hundreds of children with a rare muscle-wasting disease will be able to receive two drugs that can improve their survival in a move parents hailed as a “lifeline”. The National Institute for Health and Care Excellence (Nice) has published final draft guidance recommending that any patient who would benefit can have either drug. Continue reading...

By Denis Campbell Health policy editor